Beam Therapeutics Inc.’s base editing platform with BEAM-101 has trait-like hematology and RMAT/ODD designations. BEAM thinks this could eventually position it with a potential best-in-class SCD drug.
Beam Therapeutics' pipeline progress remains slow, with BEAM-101 still recruiting and CAR-T programs discontinued to reduce cash burn. Gene therapy markets targeted by Beam, such as SCD and AATD, are ...